BMT CTN Protocol 2001 SCD Gene Therapy

A Multi-Center, Phase 2 Gene Transfer Study Inducing Fetal Hemoglobin in Sickle Cell Disease

Below is protocol-related information that may be periodically updated.

             BMT CTN Co-Chair: David A. Williams, MD david.williams2@childrens.harvard.edu

             BMT CTN Co-Chair: Mark C. Walters, MD mark.walters@ucsf.edu

             Protocol Officer: Mary Eapen, MD meapen@mcw.edu

             Protocol Coordinator: Alyssa Ramirez aramirez@emmes.com

The BMT CTN is committed to including widespread transplant community participation in these trials. However, afflilate center applications are not currently being accepted for this study.